PTC Therapeutics plans to soon ask the FDA to approve ataluren to treat Duchenne muscular dystrophy (DMD) caused by nonsense ...
More than a half dozen exon-skipping therapies for DMD, all aiming to increase dystrophin protein production, are being ...
In a third-quarter meeting with the FDA, Capricor will discuss plans for an application seeking approval of the DMD cell ...
Columnist Betty Vertin has realized that she's not the fun mom she used to be and is taking steps to change for her younger daughters' sake.
The Parent Project Muscular Dystrophy (PPMD) 30th annual conference kicks off today, offering families affected by Duchenne muscular dystrophy (DMD) or Becker muscular dystrophy (BMD) the chance to ...
The Parent Project Muscular Dystrophy (PPMD) 30th annual conference kicks off today, offering families affected by Duchenne ...
A Phase 3 trial testing an experimental therapy for limb-girdle muscular dystrophy type 2i (LGMD2i) has surpassed patient ...
In FORTITUDE, del-brax helped adults with FSHD grow stronger muscles and reach their arms farther than they could four months ...
Parent Project Muscular Dystrophy (PPMD) held its first conference in 1994, in Orlando, Florida. A year later, at its meeting in Pittsburgh, fewer than two dozen people were in attendance, just a ...